Published: Nov 18, 2023 01:33:41 pm
Britain has approved the world’s first gene therapy to treat blood disorders such as sickle-cell and thalassemia using the gene-editing tool CRISPR, which earned its inventors the Nobel Prize in 2020.
Health update: World’s first gene therapy for the treatment of Thalassemia has arrived
Till now the only permanent treatment for thalassemia was bone marrow transplant. Which was possible only with someone close. But now the UK’s Medicines and Healthcare products Regulatory Agency has authorized a new treatment, called CasGevi, for patients aged 12 and over with sickle cell disease and transfusion-dependent beta-thalassemia. Both sickle cell disease and beta-thalassemia are genetic. There are conditions that are caused by errors in the gene for hemoglobin.